Category | Funding IC | Project Number | Sub Project # | Project Title | PI Name | Org Name | State / Country | Amount |
Muscular Dystrophy
|
NIGMS
|
5R01GM038219-20
|
|
Instability of Triplet Repeats in Mammalian Cells
|
WILSON, JOHN
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$308,050
|
Muscular Dystrophy
|
NHLBI
|
5R01HL073315-05
|
|
Functional Phenotyping of Cardiomyopathy by MRI
|
YU, XIN
|
CASE WESTERN RESERVE UNIVERSITY
|
OH
|
$362,679
|
Muscular Dystrophy
|
NHLBI
|
5R01HL082792-02
|
|
Nuclear mechanics and mechanotransduction in muscular laminopathies
|
LAMMERDING, JAN
|
BRIGHAM AND WOMEN'S HOSPITAL
|
MA
|
$258,000
|
Muscular Dystrophy
|
NIGMS
|
5R01GM063066-07
|
|
Fragility and Instability at Hairpin-Forming Trinucleotide Repeats in Yeast
|
FREUDENREICH, CATHERINE
|
TUFTS UNIVERSITY MEDFORD
|
MA
|
$309,001
|
Muscular Dystrophy
|
NIMH
|
5R01MH077303-03
|
|
Neurexins: synaptic building blocks
|
RUDENKO, GABRIELLE
|
UNIVERSITY OF MICHIGAN AT ANN ARBOR
|
MI
|
$250,906
|
Muscular Dystrophy
|
NIAMS
|
5R01AR049899-05
|
|
Costamere Defects in Muscular Dystrophies
|
ERVASTI, JAMES
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$336,457
|
Muscular Dystrophy
|
NCI
|
5R01CA109579-04
|
|
Dystroglycan in Epithelial Architecture and Function
|
MUSCHLER, JOHN
|
CALIFORNIA PACIFIC MED CTR RES INSTITUTE
|
CA
|
$290,637
|
Muscular Dystrophy
|
NINDS
|
1R01NS060839-01
|
|
Biochemical analyses of muscleblind complexes in myotonic dystrophy
|
REDDY, SITA
|
UNIVERSITY OF SOUTHERN CALIFORNIA
|
CA
|
$479,733
|
Muscular Dystrophy
|
NINDS
|
5R01NS056592-02
|
|
Structural and Functional CNS Changes in Myotonic Dystrophy Types 1 and 2
|
DAY, JOHN
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$322,618
|
Muscular Dystrophy
|
NIAMS
|
1R21AR055704-01
|
|
Role of Narexin in Neuromuscular Disease
|
ISACKSON, PAUL
|
STATE UNIVERSITY OF NEW YORK AT BUFFALO
|
NY
|
$174,350
|
Muscular Dystrophy
|
NIAMS
|
1R21AR055725-01
|
|
Use of matrix metalloproteinase to improve myogenic cell transplantation in MDX m
|
LI, YONG
|
CHILDREN'S HOSP PITTSBURGH/UPMC HLTH SYS
|
PA
|
$179,850
|
Muscular Dystrophy
|
NINDS
|
5K08NS051349-03
|
|
Myoregenerative Potential of ABCB5+ Progenitors
|
FRANK, NATASHA
|
BRIGHAM AND WOMEN'S HOSPITAL
|
MA
|
$133,920
|
Muscular Dystrophy
|
NHLBI
|
5R01HL064641-09
|
|
Molecular physiology of respiratory muscles
|
MILLER, JEFFREY
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$501,842
|
Muscular Dystrophy
|
NIAMS
|
5R01AR051440-03
|
|
Muscle Cell Signaling
|
JARRETT, HARRY
|
UNIVERSITY OF TEXAS SAN ANTONIO
|
TX
|
$236,981
|
Muscular Dystrophy
|
NINDS
|
5K08NS049346-03
|
|
Role of TGF-B1 in Duchenne Muscular Dystrophy
|
ZHOU, LAN
|
CLEVELAND CLINIC LERNER COL/MED-CWRU
|
OH
|
$169,668
|
Muscular Dystrophy
|
NIAMS
|
5R01AR052027-02
|
|
Molecular Pathphysiology of FSHD muscular dystrophy via genome-wide approaches
|
CHEN, YI-WEN
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$349,762
|
Muscular Dystrophy
|
NIAMS
|
5R01AR053242-03
|
|
Immune Tolerence to Transplanted Myoblasts
|
ROTHSTEIN, DAVID
|
YALE UNIVERSITY
|
CT
|
$290,704
|
Muscular Dystrophy
|
NINDS
|
5R21NS057516-02
|
|
A Mouse Model of RNA-induced Neurotoxcity
|
MARGOLIS, RUSSELL
|
JOHNS HOPKINS UNIVERSITY
|
MD
|
$215,250
|
Muscular Dystrophy
|
NIAMS
|
5R01AR050202-05
|
|
Galgt2, dystroglycan, and muscle extracellular matrix
|
MARTIN, PAUL
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$261,259
|
Muscular Dystrophy
|
NIAMS
|
2K24AR048143-06
|
|
Integrative Pathophysiology of Myotonic Dystrophy
|
THORNTON, CHARLES
|
UNIVERSITY OF ROCHESTER
|
NY
|
$125,253
|
Muscular Dystrophy
|
NIAMS
|
1R21AR056480-01A1
|
|
IGF-I isoforms: a source for new agents to counter muscular dystrophy pathology
|
BARTON, ELISABETH
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$207,900
|
Muscular Dystrophy
|
NINDS
|
5R01NS029525-16
|
|
Improved Diagnostic of the Muscular Dystrophies
|
HOFFMAN, ERIC
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$538,241
|
Muscular Dystrophy
|
NINDS
|
5K08NS048180-04
|
|
Anatomic variations in muscle gene expression
|
KANG, PETER
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$168,107
|
Muscular Dystrophy
|
NIAMS
|
5R01AR051199-05
|
|
Therapeutic Potentential of Epsilon-Sarcoglycan in LGMD Type 2D
|
CAMPBELL, KEVIN
|
UNIVERSITY OF IOWA
|
IA
|
$322,090
|
Muscular Dystrophy
|
NIAMS
|
5R37AR040864-19
|
|
Dystrophin Replacement in mdx mice
|
CHAMBERLAIN, JEFFREY
|
UNIVERSITY OF WASHINGTON
|
WA
|
$504,779
|
Muscular Dystrophy
|
NIDDK
|
1R41DK076516-01A2
|
|
A novel approach for gene therapy
|
MAAS, STEFAN
|
ATIGEN
|
PA
|
$139,916
|
Muscular Dystrophy
|
NIAMS
|
5R01AR045653-10
|
|
Molecular Pathogenesis of Myotonic Dystrophy
|
COOPER, THOMAS
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$462,569
|
Muscular Dystrophy
|
NIAMS
|
5R01AR049722-03
|
|
Glycosyltransferase Therapy for Myopathies
|
MARTIN, PAUL
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$297,273
|
Muscular Dystrophy
|
NIAMS
|
5R01AR051368-04
|
|
Apoptosis in Laminin alpha2-Deficient Muscle Pathology
|
DOMINOV, JANICE
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$358,771
|
Muscular Dystrophy
|
NIAMS
|
5R01AR046799-09
|
|
RNA Dominance in Human Disease
|
SWANSON, MAURICE
|
UNIVERSITY OF FLORIDA
|
FL
|
$297,443
|
Muscular Dystrophy
|
NIAMS
|
5R01AR044533-13
|
|
Assembly of the Dystrophin-Glycoprotein Complex
|
CHAMBERLAIN, JEFFREY
|
UNIVERSITY OF WASHINGTON
|
WA
|
$328,692
|
Muscular Dystrophy
|
NIAMS
|
5R01AR042423-14
|
|
Cytoskeletal interactions of Dystrophin
|
ERVASTI, JAMES
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$294,551
|
Muscular Dystrophy
|
NIAMS
|
5R01AR046806-08
|
|
Pathogenesis of Myopathy in Models of Myotonic Dystrophy
|
THORNTON, CHARLES
|
UNIVERSITY OF ROCHESTER
|
NY
|
$318,908
|
Muscular Dystrophy
|
NINDS
|
1F30NS061358-01
|
|
Therapeutic application for a cell culture model of myotonic dystrophy
|
KOSHELEV, MISHA
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$32,772
|
Muscular Dystrophy
|
NIAMS
|
5R01AR048871-06
|
|
Regulation of Utrophin Promoter in Muscle
|
KHURANA, TEJVIR
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$286,646
|
Muscular Dystrophy
|
NIAMS
|
5R21AR055712-02
|
|
Muscle-specific AAV Vectors for DMD Gene Therapy
|
SAMULSKI, RICHARD
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$153,811
|
Muscular Dystrophy
|
NEI
|
5R01EY012949-09
|
|
Physiology of potassium channels in retinal glial cells
|
KOFUJI, PAULO
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$313,209
|
Muscular Dystrophy
|
NIAMS
|
5R01AR051034-05
|
|
Ischemia and the Pathogenesis of Muscular Dystrophy
|
THOMAS, GAIL
|
UNIVERSITY OF TEXAS SW MED CTR/DALLAS
|
TX
|
$296,801
|
Muscular Dystrophy
|
NINDS
|
1F31NS056780-01A2
|
|
Inducing Tolerance to Gene Transfer in Dystrophic Mice
|
EGHTESAD, SAMAN
|
UNIVERSITY OF PITTSBURGH AT PITTSBURGH
|
PA
|
$40,972
|
Muscular Dystrophy
|
NINDS
|
5R01NS033145-14
|
|
Regulation of Syntrophin Function
|
FROEHNER, STANLEY
|
UNIVERSITY OF WASHINGTON
|
WA
|
$332,409
|
Muscular Dystrophy
|
NIAMS
|
5R01AR050595-06
|
|
Gene Therapy for a severe DMD Animal Model
|
XIAO, XIAO
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$297,689
|
Muscular Dystrophy
|
NINDS
|
5R01NS043264-06
|
|
Translational Research in the Dystrophinopathies
|
FLANIGAN, KEVIN
|
UNIVERSITY OF UTAH
|
UT
|
$913,423
|
Muscular Dystrophy
|
NIAMS
|
5K23AR053197-03
|
|
Idiopathic Inflammatory Myopathies: Improving Diagnosis and Predicting Outcomes
|
CHRISTOPHER-STINE, LISA
|
JOHNS HOPKINS UNIVERSITY
|
MD
|
$136,358
|
Muscular Dystrophy
|
NINDS
|
5R01NS048859-05
|
|
FSHD: Chromatin Structure, Looping, & Expression
|
EHRLICH, MELANIE
|
TULANE UNIVERSITY OF LOUISIANA
|
LA
|
$293,050
|
Muscular Dystrophy
|
NINDS
|
5R01NS050861-03
|
|
Molecular Mechanisms Underlying DM1
|
REDDY, SITA
|
UNIVERSITY OF SOUTHERN CALIFORNIA
|
CA
|
$356,114
|
Muscular Dystrophy
|
NIAMS
|
5R03AR054084-03
|
|
Regulation of Oxidative Stress in the mdx Diaphragm
|
LAWLER, JOHN
|
TEXAS A&M UNIVERSITY SYSTEM
|
TX
|
$66,360
|
Muscular Dystrophy
|
NICHD
|
5R01HD053728-03
|
|
Muscle and Muscle Connective Tissue Development in the Vertebrate Llmb
|
KARDON, GABRIELLE
|
UNIVERSITY OF UTAH
|
UT
|
$298,749
|
Muscular Dystrophy
|
NIAMS
|
5F32AR053803-03
|
|
Role of PPAR-delta in Duchenne Muscular Dystrophy
|
NARKAR, VIHANG
|
SALK INSTITUTE FOR BIOLOGICAL STUDIES
|
CA
|
$56,702
|
Muscular Dystrophy
|
NIAMS
|
5R01AR052791-04
|
|
Myotonic Dystrophy Type 2
|
TIMCHENKO, LUBOV
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$275,978
|
Muscular Dystrophy
|
NIAMS
|
5R03AR054955-02
|
|
Adult muscle stem cells as cell therapy in utrophin-dystrophin deficient mice
|
REYES, MORAYMA
|
UNIVERSITY OF WASHINGTON
|
WA
|
$81,340
|
Muscular Dystrophy
|
NIGMS
|
1R01GM086167-01
|
|
Intracellular calcium signaling in normal and diseased mammalian skeletal muscle
|
BAYLOR, STEPHEN
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$315,000
|
Muscular Dystrophy
|
NHLBI
|
5R01HL063134-08
|
|
Physiology of Respiratory Muscle Micromechanics
|
BORIEK, ALADIN
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$399,263
|
Muscular Dystrophy
|
NINDS
|
5R21NS058345-02
|
|
Therapeutic approach targeting RNA disease in myotonic dystrophy
|
THORNTON, CHARLES
|
UNIVERSITY OF ROCHESTER
|
NY
|
$199,365
|
Muscular Dystrophy
|
NIGMS
|
1R01GM084085-01
|
|
SUN-nesprin complexes in human laminopathies
|
BURKE, BRIAN
|
UNIVERSITY OF FLORIDA
|
FL
|
$304,397
|
Muscular Dystrophy
|
NINDS
|
5R21NS059399-02
|
|
Genetic analysis of FRG1 function in Drosophila
|
MATTOX, WILLIAM
|
UNIVERSITY OF TEXAS MD ANDERSON CAN CTR
|
TX
|
$168,438
|
Muscular Dystrophy
|
NIAMS
|
1K23AR055947-01
|
|
The Development and Use of a Disease-Specific Instrument for Myotonic Dystophy
|
HEATWOLE, CHAD
|
UNIVERSITY OF ROCHESTER
|
NY
|
$129,551
|
Muscular Dystrophy
|
NHLBI
|
1R01HL092443-01
|
|
Nuclear membrane protein interaction in heart and muscle disease
|
MCNALLY, ELIZABETH
|
UNIVERSITY OF CHICAGO
|
IL
|
$378,614
|
Muscular Dystrophy
|
NINDS
|
5F31NS058224-02
|
|
Delivery of a Myostatin Inhibitor by AAV Gene Therapy for Muscular Dystrophy
|
HAIDET, AMANDA
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$31,003
|
Muscular Dystrophy
|
NHLBI
|
5R01HL080388-03
|
|
Cardiomyopathy in muscular dystrophies
|
MICHELE, DANIEL
|
UNIVERSITY OF MICHIGAN AT ANN ARBOR
|
MI
|
$323,498
|
Muscular Dystrophy
|
NIAMS
|
5K01AR052372-03
|
|
Improving cell therapy using L-selectin homing
|
WESTERMAN, KAREN
|
BRIGHAM AND WOMEN'S HOSPITAL
|
MA
|
$128,930
|
Muscular Dystrophy
|
NIAMS
|
5R01AR050565-05
|
|
Genetic Rescue of Dystrophic Muscle In Utero
|
CLEMENS, PAULA
|
UNIVERSITY OF PITTSBURGH AT PITTSBURGH
|
PA
|
$219,858
|
Muscular Dystrophy
|
NIAMS
|
1R03AR056107-01
|
|
Development of RNA interference for treatment of myotonic dystrophy in the HSALR
|
CHAMBERLAIN, JOEL
|
UNIVERSITY OF WASHINGTON
|
WA
|
$78,000
|
Muscular Dystrophy
|
NIAMS
|
5R01AR051999-04
|
|
The Molecular Basis of CMD Types Ullrich and Bethlem
|
BONNEMANN, CARSTEN
|
CHILDREN'S HOSPITAL OF PHILADELPHIA
|
PA
|
$339,350
|
Muscular Dystrophy
|
NHLBI
|
2R01HL045565-18
|
|
Troponin T Alternative Splicing in Embryonic Heart
|
COOPER, THOMAS
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$383,750
|
Muscular Dystrophy
|
NIA
|
5R01AG024987-05
|
|
Regulator of Adult Stem Cell Fate
|
BLAU, HELEN
|
STANFORD UNIVERSITY
|
CA
|
$300,216
|
Muscular Dystrophy
|
NIAMS
|
5R01AR053970-03
|
|
Structure of the dystrophin rod in relation to exon boundaries and exon skipping
|
MENHART, NICK
|
ILLINOIS INSTITUTE OF TECHNOLOGY
|
IL
|
$136,327
|
Muscular Dystrophy
|
NIAMS
|
1R01AR053697-01A2
|
|
Integrin Alleviation of Muscular Dystrophy
|
BURKIN, DEAN
|
UNIVERSITY OF NEVADA RENO
|
NV
|
$247,133
|
Muscular Dystrophy
|
NIAMS
|
5F32AR054219-04
|
|
Role of Lmo7 in Emery-Dreifuss muscular dystrophy
|
WOZNIAK, MICHELE
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$50,428
|
Muscular Dystrophy
|
NIAMS
|
1R21AR056628-01A1
|
|
A Combinatorial Strategy to Treat Congenital Muscular Dystrophy
|
GIRGENRATH, MAHASWETA
|
BOSTON UNIVERSITY
|
MA
|
$178,750
|
Muscular Dystrophy
|
NEI
|
1R21EY018112-01A1
|
|
Temporal and Spatial patterns of structural proteins in extraocular muscles
|
MONCMAN, CAROLE
|
UNIVERSITY OF KENTUCKY
|
KY
|
$219,750
|
Muscular Dystrophy
|
NINDS
|
1R21NS059514-01A1
|
|
cGMP Phosphodiesterase Inhibitors in a Mouse Model of Duchenne Muscular Dystrophy
|
FROEHNER, STANLEY
|
UNIVERSITY OF WASHINGTON
|
WA
|
$204,750
|
Muscular Dystrophy
|
NHLBI
|
1R21HL089684-01A1
|
|
Sonic Muscle Regeneration
|
POLA, ROBERTO
|
CARITAS ST. ELIZABETH'S MEDICAL CENTER
|
MA
|
$212,500
|
Muscular Dystrophy
|
NIAMS
|
2R01AR049419-06
|
|
Dual AAV Vectors for Duchenne Muscular Dystrophy Therapy
|
DUAN, DONGSHENG
|
UNIVERSITY OF MISSOURI-COLUMBIA
|
MO
|
$438,213
|
Muscular Dystrophy
|
NIAMS
|
1R21AR055231-01A1
|
|
Functional Analysis of ZNF9 in Myotonic Dystrophy Type 2
|
LINK, ANDREW
|
VANDERBILT UNIVERSITY
|
TN
|
$168,850
|
Muscular Dystrophy
|
NIAMS
|
5R03AR053678-02
|
|
Expansion of Post-natal Human Stem Cells For A Pre-Clinical Dystrophy Model
|
DEASY, BRIDGET
|
CHILDREN'S HOSP PITTSBURGH/UPMC HLTH SYS
|
PA
|
$70,315
|
Muscular Dystrophy
|
NIAMS
|
5K08AR052308-04
|
|
Creative biosynthesis mitigates pathogenesis in mdx mice
|
TSENG, BRIAN
|
MASSACHUSETTS GENERAL HOSPITAL
|
MA
|
$126,900
|
Muscular Dystrophy
|
NINDS
|
5R01NS045630-06
|
|
Laminin receptors and signals in Schwann cells
|
FELTRI, MARIA
|
FONDAZONE CENT/SAN RAFFAELE/DEL MONTE
|
ITALY
|
$236,250
|
Muscular Dystrophy
|
NHLBI
|
5R01HL081753-04
|
|
Genetic Studies of Sarcomere-based Cardiac Diseases
|
XU, XIAOLEI
|
MAYO CLINIC COLL OF MEDICINE, ROCHESTER
|
MN
|
$348,551
|
Muscular Dystrophy
|
NIAMS
|
5R01AR045967-10
|
|
AAV Vectors for Heart and Muscle Gene Therapy
|
XIAO, XIAO
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$302,982
|
Muscular Dystrophy
|
NIAMS
|
5R01AR053903-03
|
|
Molecular Mechanisms of Myotonic Dystrophy
|
BERGLUND, JOHN
|
UNIVERSITY OF OREGON
|
OR
|
$242,359
|
Muscular Dystrophy
|
NIAMS
|
5K08AR050966-03
|
|
Analyzing Zmpste24 Deficiency in Mice
|
META, MARGARITA
|
UNIVERSITY OF CALIFORNIA LOS ANGELES
|
CA
|
$116,370
|
Muscular Dystrophy
|
NIAMS
|
5R01AR052693-02
|
|
Pathogenic Mechanisms in Limb Girdle Muscular Dystrophies
|
SPENCER, MELISSA
|
UNIVERSITY OF CALIFORNIA LOS ANGELES
|
CA
|
$353,696
|
Muscular Dystrophy
|
NIAMS
|
1R41AR055604-01A2
|
|
Automated analysis of skeletal muscle fiber crossectional area and metabolic type
|
MCDONOUGH, PATRICK
|
VALA SCIENCES, INC.
|
CA
|
$153,853
|
Muscular Dystrophy
|
NIAMS
|
5K02AR051181-05
|
|
Strategies to improve stem cell engraftment into muscle
|
WANG, YAMING
|
BRIGHAM AND WOMEN'S HOSPITAL
|
MA
|
$106,920
|
Muscular Dystrophy
|
NIAMS
|
5R01AR054366-02
|
|
Muscle protein synthesis and gene expression in myostatin-deficient mice
|
WELLE, STEPHEN
|
UNIVERSITY OF ROCHESTER
|
NY
|
$264,003
|
Muscular Dystrophy
|
NIAMS
|
5R01AR052771-04
|
|
Inducible Transgenic Mouse Model of RNA Toxicity
|
MAHADEVAN, MANI
|
UNIVERSITY OF VIRGINIA CHARLOTTESVILLE
|
VA
|
$309,708
|
Muscular Dystrophy
|
NIAMS
|
5R21AR055878-02
|
|
Testing a Novel DMD Therapeutic in MDX Mice
|
FALLON, JUSTIN
|
BROWN UNIVERSITY
|
RI
|
$127,267
|
Muscular Dystrophy
|
NCI
|
1R13CA134185-01
|
|
RNA and the Etiology of Disease
|
RICHTER, JOEL
|
UNIV OF MASSACHUSETTS MED SCH WORCESTER
|
MA
|
$6,000
|
Muscular Dystrophy
|
NIAMS
|
1R13NS062636-01
|
|
New Directions in Biology and Disease of Skeletal Muscle
|
MCNALLY, ELIZABETH
|
UNIVERSITY OF CHICAGO
|
IL
|
$5,000
|
Muscular Dystrophy
|
NICHD
|
1R13NS062636-01
|
|
New Directions in Biology and Disease of Skeletal Muscle
|
MCNALLY, ELIZABETH
|
UNIVERSITY OF CHICAGO
|
IL
|
$3,000
|
Muscular Dystrophy
|
NINDS
|
1R13NS062636-01
|
|
New Directions in Biology and Disease of Skeletal Muscle
|
MCNALLY, ELIZABETH
|
UNIVERSITY OF CHICAGO
|
IL
|
$7,000
|
Muscular Dystrophy
|
OD
|
1R13NS062636-01
|
|
New Directions in Biology and Disease of Skeletal Muscle
|
MCNALLY, ELIZABETH
|
UNIVERSITY OF CHICAGO
|
IL
|
$25,000
|
Muscular Dystrophy
|
NHLBI
|
5DP1OD000392-04
|
|
NIH Director's Pioneer Award (RMI)
|
RANDO, THOMAS
|
PALO ALTO INSTITUTE FOR RES & EDU, INC.
|
CA
|
$341,775
|
Muscular Dystrophy
|
NIA
|
5DP1OD000392-04
|
|
NIH Director's Pioneer Award (RMI)
|
RANDO, THOMAS
|
PALO ALTO INSTITUTE FOR RES & EDU, INC.
|
CA
|
$341,775
|
Muscular Dystrophy
|
NIAMS
|
5R01AR048177-08
|
|
LGMD 2A Protein Calpain 3 and Its Binding to Titin
|
SPENCER, MELISSA
|
UNIVERSITY OF CALIFORNIA LOS ANGELES
|
CA
|
$368,745
|
Muscular Dystrophy
|
NINDS
|
1F30NS057884-01A2
|
|
Investigating mechanisms of skeletal muscle degeneration in Myotonic Dystrophy
|
ORENGO, JAMES
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$35,990
|
Muscular Dystrophy
|
NINDS
|
5U01NS052476-02
|
|
Translational program for molecular therapeutics in DMD
|
STEDMAN, HANSELL
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$983,535
|
Muscular Dystrophy
|
NEI
|
5R01EY013862-05
|
|
Molecular Characterization of Extraocular Muscle
|
KHURANA, TEJVIR
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$377,076
|
Muscular Dystrophy
|
NHLBI
|
5R01HL086790-02
|
|
Chemical-based membrane sealants for dystrophic muscle
|
METZGER, JOSEPH
|
UNIVERSITY OF MICHIGAN AT ANN ARBOR
|
MI
|
$453,020
|
Muscular Dystrophy
|
NIAMS
|
5R01AR055877-02
|
|
Molecular mechanism of FSHD pathology
|
JONES, PETER
|
UNIVERSITY OF ILLINOIS URBANA-CHAMPAIGN
|
IL
|
$253,022
|
Muscular Dystrophy
|
NINDS
|
5K08NS055879-03
|
|
Role of TGFB signaling in muscle regeneration and various myopathic states
|
COHN, RONALD
|
JOHNS HOPKINS UNIVERSITY
|
MD
|
$176,994
|
Muscular Dystrophy
|
NINDS
|
5R01NS059352-02
|
|
Nucleocytoplasmic Interactions and Dynamics in Emery-Dreifuss Muscular Dystrophy
|
WORMAN, HOWARD
|
COLUMBIA UNIVERSITY HEALTH SCIENCES
|
NY
|
$352,188
|
Muscular Dystrophy
|
NINDS
|
5R01NS059348-02
|
|
Nuclear-cytoskeletal coupling in muscular laminopathies
|
LAMMERDING, JAN
|
BRIGHAM AND WOMEN'S HOSPITAL
|
MA
|
$264,031
|
Muscular Dystrophy
|
NIGMS
|
5R01GM081775-02
|
|
Dystroglycan in Epithelial and Neural Development
|
KRAMER, JAMES
|
NORTHWESTERN UNIVERSITY
|
IL
|
$264,250
|
Muscular Dystrophy
|
NIAMS
|
5R21AR055879-02
|
|
Sequence Specific Targeting of poly-CUG Motifs
|
MELANDER, CHRISTIAN
|
NORTH CAROLINA STATE UNIVERSITY RALEIGH
|
NC
|
$159,284
|
Muscular Dystrophy
|
NICHD
|
5F32HD055011-02
|
|
Molecular mechanisms regulating muscle patterning
|
BERES, THOMAS
|
UNIVERSITY OF UTAH
|
UT
|
$51,278
|
Muscular Dystrophy
|
NIAMS
|
5R21AR055876-02
|
|
FSHD as a Disorder of Impaired RNA Biogenesis
|
VAN DER MAAREL, SILVERE
|
LEIDEN UNIVERSITY MEDICAL CENTER
|
NETH
|
$136,534
|
Muscular Dystrophy
|
NINDS
|
5R21NS059366-02
|
|
Model of OPMD with constitutive PABPN1 expression
|
THORNTON, CHARLES
|
UNIVERSITY OF ROCHESTER
|
NY
|
$168,438
|
Muscular Dystrophy
|
NIAMS
|
5R01AR049077-06
|
|
RNA-mediated mechanisms in the myotonic dystrophies
|
THORNTON, CHARLES
|
UNIVERSITY OF ROCHESTER
|
NY
|
$324,478
|
Muscular Dystrophy
|
NIAMS
|
5F31AR054724-03
|
|
Immune and muscle cell interactions that modulate dystrophinopathy
|
VILLALTA, SERGIO
|
UNIVERSITY OF CALIFORNIA LOS ANGELES
|
CA
|
$31,038
|
Muscular Dystrophy
|
NIAMS
|
5R01AR056129-02
|
|
An Animal model to develop therapeutic strategies for FSHD
|
TUPLER, ROSSELLA
|
UNIV OF MASSACHUSETTS MED SCH WORCESTER
|
MA
|
$336,699
|
Muscular Dystrophy
|
NIAMS
|
5F32AR054699-02
|
|
A therapeutic approach to muscle wasting by limiting protein breakdown
|
BRAULT, JEFFREY
|
HARVARD UNIVERSITY (MEDICAL SCHOOL)
|
MA
|
$54,842
|
Muscular Dystrophy
|
NIAMS
|
5F32AR055008-02
|
|
Dystrophin restoration in two animal models of Duchenne Muscular Dystrophy
|
RODINO, LOUISE
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$49,646
|
Muscular Dystrophy
|
NIAMS
|
5R01AR054170-02
|
|
Genetic Control of Phospholipid Biosynthesis and Muscular Dystrophy
|
COX, GREGORY
|
JACKSON LABORATORY
|
ME
|
$349,931
|
Muscular Dystrophy
|
NIAMS
|
5F32AR055005-02
|
|
Does catalase expression improve the function muscles from of mdx and LGMD mice?
|
SELSBY, JOSHUA
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$12,715
|
Muscular Dystrophy
|
NINDS
|
1P01NS058901-01A1
|
0001
|
Temporal/spatial RNA Expression Effects in DM1 and DM2
|
RANUM, LAURA
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$443,814
|
Muscular Dystrophy
|
NINDS
|
1P01NS058901-01A1
|
0002
|
Mechanisms of RNA-mediated CMS Pathogenesis in Myotonic Dystrophy
|
SWANSON, MAURICE
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$378,240
|
Muscular Dystrophy
|
NINDS
|
1P01NS058901-01A1
|
0003
|
Structural and Functional CMS Changes in Children with Myotonic Dystrophy
|
DAY, JOHN
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$205,015
|
Muscular Dystrophy
|
NINDS
|
1P01NS058901-01A1
|
9001
|
Neuropathology and Optical Imaging Core
|
CLARK, H.
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$206,170
|
Muscular Dystrophy
|
NIGMS
|
5R01GM036643-23
|
|
Recognition of Regulatory and Pathogenic RNA by Muscleblind Zinc Fingers
|
WRIGHT, PETER
|
SCRIPPS RESEARCH INSTITUTE
|
CA
|
$473,750
|
Muscular Dystrophy
|
NINDS
|
5R01NS058814-02
|
|
Identification of Novel Components of the Dystrophin Complex Using C. Elegans
|
KIM, HONGKYUN
|
ERNEST GALLO CLINIC AND RESEARCH CENTER
|
CA
|
$273,000
|
Muscular Dystrophy
|
NINDS
|
5R01NS058382-02
|
|
Cellular Nucleic Acid Binding Protein (CNBP) in Aging and Disease
|
MURPHY, MICHAEL
|
UNIVERSITY OF KENTUCKY
|
KY
|
$288,422
|
Muscular Dystrophy
|
NINDS
|
5R21NS058429-02
|
|
A drug-based approach for integrin-mediated alleviation of muscular dystrophy
|
BURKIN, DEAN
|
UNIVERSITY OF NEVADA RENO
|
NV
|
$215,141
|
Muscular Dystrophy
|
NINDS
|
1R21NS062934-01
|
|
Expressing full-length dystrophin with AAV
|
DUAN, DONGSHENG
|
UNIVERSITY OF MISSOURI-COLUMBIA
|
MO
|
$163,516
|
Muscular Dystrophy
|
NINDS
|
1R03NS063298-01
|
|
Mechanisms of decay of toxic CUGn RNA in DM1 patients
|
TIMCHENKO, LUBOV
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$76,750
|
Muscular Dystrophy
|
NIDDK
|
2R01DK063945-05A1
|
|
Biotin Deficiency Impairs Silencing of Repeat Regions & Retrotransposons
|
ZEMPLENI, JANOS
|
UNIVERSITY OF NEBRASKA LINCOLN
|
NE
|
$313,502
|
Muscular Dystrophy
|
NINDS
|
1R21NS058926-01A2
|
|
Stakeholders' Views on Research Design: The Duchenne Muscular Dystrophy Community
|
NELSON, ROBERT
|
CHILDREN'S HOSPITAL OF PHILADELPHIA
|
PA
|
$179,922
|
Muscular Dystrophy
|
NIAMS
|
1R21AR054427-01A2
|
|
Role of Calpains in Plasma Membrane Repair
|
MELLGREN, RONALD
|
UNIVERSITY OF TOLEDO HEALTH SCI CAMPUS
|
OH
|
$206,073
|
Muscular Dystrophy
|
NIAMS
|
1R21AR054746-01A2
|
|
Conversion of pre-adipose cells into muscle cells
|
DERYNCK, RIK
|
UNIVERSITY OF CALIFORNIA SAN FRANCISCO
|
CA
|
$203,940
|
Muscular Dystrophy
|
NIAMS
|
1R21AR053901-01A2
|
|
Does sleep apnea exacerbate respiratory muscle dysfunction in muscular dystrophy?
|
FARKAS, GASPAR
|
STATE UNIVERSITY OF NEW YORK AT BUFFALO
|
NY
|
$209,220
|
Muscular Dystrophy
|
NINDS
|
1R21NS058336-01A2
|
|
Gene Therapy for Muscular Dystrophy
|
CHAO, HENGJUN
|
MOUNT SINAI SCHOOL OF MEDICINE OF NYU
|
NY
|
$191,893
|
Muscular Dystrophy
|
NIAMS
|
1K99AR054793-01A2
|
|
Calcium Regulation in the Progression of Muscular Dystrophy
|
WEISLEDER, NOAH
|
UNIV OF MED/DENT NJ-R W JOHNSON MED SCH
|
NJ
|
$79,731
|
Muscular Dystrophy
|
NIAMS
|
1R01AR055686-01A2
|
|
Understanding the mechanism and role of cell membrane repair in Miyoshi Myopathy
|
JAISWAL, JYOTI
|
ROCKEFELLER UNIVERSITY
|
NY
|
$314,688
|
Muscular Dystrophy
|
NIAMS
|
1U54AR056953-01
|
9002
|
National Canine Muscular Dystrophy Core
|
KORNEGAY, JOE
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$90,744
|
Muscular Dystrophy
|
NIAMS
|
1U54AR056953-01
|
9003
|
National Vector Muscular Dystrophy Core
|
BEECHAM, JEFFREY
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$311,092
|
Muscular Dystrophy
|
NIAMS
|
1U54AR056953-01
|
0001
|
Safety and Feasibility Study of Transvenous Limb Perfusion with Normal Saline in
|
POWERS, WILLIAM
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$243,326
|
Muscular Dystrophy
|
NIAMS
|
1U54AR056953-01
|
0002
|
Gene therapy in golden retriever muscular dystrophy model
|
XIAO, XIAO
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$349,687
|
Muscular Dystrophy
|
NIAMS
|
1U54AR056953-01
|
0003
|
Adeno-associated Virus Vectors for Targeted and Repeat Delivery
|
SAMULSKI, RICHARD
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$337,966
|
Muscular Dystrophy
|
NINDS
|
2U54NS048843-06
|
0004
|
Overall Review
|
MOXLEY, RICHARD T
|
UNIVERSITY OF ROCHESTER
|
NY
|
$2,772
|
Muscular Dystrophy
|
NINDS
|
2U54NS048843-06
|
9004
|
Repository and Registry of Myotonic Dystrophy Core
|
MOXLEY, RICHARD
|
UNIVERSITY OF ROCHESTER
|
NY
|
$52,060
|
Muscular Dystrophy
|
NINDS
|
2U54NS048843-06
|
0005
|
Disease Progression in Myotonic Dystrophy
|
MOXLEY, RICHARD
|
UNIVERSITY OF ROCHESTER
|
NY
|
$623,379
|
Muscular Dystrophy
|
NINDS
|
2U54NS048843-06
|
0006
|
Experimental Therapy of Myotonic Dystrophy
|
THORNTON, CHARLES
|
UNIVERSITY OF ROCHESTER
|
NY
|
$655,953
|
Muscular Dystrophy
|
NIAMS
|
1R21AR056128-01A1
|
|
Matrix-induced Myogenesis & Pharmaco-Screens of MSCs
|
DISCHER, DENNIS
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$199,391
|
Muscular Dystrophy
|
NICHD
|
1U54HD060848-01
|
5181
|
Administrative Core
|
EMERSON, CHARLES
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$77,864
|
Muscular Dystrophy
|
NICHD
|
1U54HD060848-01
|
0001
|
Clinical Trials and Biomarkers of Myostatin Inhibition
|
WAGNER, KATHERINE
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$90,415
|
Muscular Dystrophy
|
NICHD
|
1U54HD060848-01
|
0002
|
Biomarker Discovery in Muscules from FSHD Patients
|
KUNKEL, LOUIS
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$327,049
|
Muscular Dystrophy
|
NICHD
|
1U54HD060848-01
|
0003
|
Myogenesis Studies for FSHD Biomarkers
|
EMERSON, CHARLES
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$322,994
|
Muscular Dystrophy
|
NICHD
|
1U54HD060848-01
|
0004
|
Model Studies for FSHD Biomarkers
|
MILLER, JEFFREY
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$269,265
|
Muscular Dystrophy
|
NHLBI
|
3R01HL054887-13S1
|
|
Mechanical Transduction by Cardiocytes
|
SACHS, FREDERICK
|
STATE UNIVERSITY OF NEW YORK AT BUFFALO
|
NY
|
$3,714
|
Muscular Dystrophy
|
NINDS
|
1U44NS060181-01A1
|
|
Preclinical Studies Supporting Phase Ib Study of Minidystrophin Gene in AAV Vecto
|
MCPHEE, SCOTT
|
ASKLEPIOS BIOPHARMACEUTICAL, INC.
|
NC
|
$320,998
|
Muscular Dystrophy
|
NIAMS
|
1R13AR056530-01
|
|
Congenital Muscular Dystrophy Workshop
|
MOORE, STEVEN
|
UNIVERSITY OF IOWA
|
IA
|
$15,000
|
Muscular Dystrophy
|
NINDS
|
1R13AR056530-01
|
|
Congenital Muscular Dystrophy Workshop
|
MOORE, STEVEN
|
UNIVERSITY OF IOWA
|
IA
|
$5,000
|
Muscular Dystrophy
|
OD
|
1R13AR056530-01
|
|
Congenital Muscular Dystrophy Workshop
|
MOORE, STEVEN
|
UNIVERSITY OF IOWA
|
IA
|
$16,280
|
Muscular Dystrophy
|
NINDS
|
1K08NS064293-01
|
|
EXPERIMENTAL THERAPEUTICS IN MOUSE MODELS OF MYOTONIC DYSTROPHY
|
WHEELER, THURMAN
|
UNIVERSITY OF ROCHESTER
|
NY
|
$159,011
|
Muscular Dystrophy
|
NIAMS
|
1R01AR053933-01A2
|
|
Mitochondria and calcium signaling in skeletal muscle
|
SHIROKOVA, NATALIA
|
UNIV OF MED/DENT OF NJ-NJ MEDICAL SCHOOL
|
NJ
|
$330,880
|
Muscular Dystrophy
|
NINDS
|
5P01NS046788-05
|
0001
|
Dystrophin Delivery to Muscle via Myogenic Precursors
|
CHAMBERLAIN, JEFFREY
|
UNIVERSITY OF WASHINGTON
|
WA
|
$610,728
|
Muscular Dystrophy
|
NINDS
|
5P01NS046788-05
|
0002
|
Signalling via Dystrobrevin in Muscular Dystrophy
|
FROEHNER, STANLEY
|
UNIVERSITY OF WASHINGTON
|
WA
|
$280,088
|
Muscular Dystrophy
|
NINDS
|
5P01NS046788-05
|
0003
|
Cell Culture Models for Testing Dystrophobic Muscle Gene Therapy
|
HAUSCHKA, STEPHEN
|
UNIVERSITY OF WASHINGTON
|
WA
|
$272,454
|
Muscular Dystrophy
|
NINDS
|
5P01NS046788-05
|
9001
|
Core--Mouse Biology
|
CHAMBERLAIN, JEFFREY
|
UNIVERSITY OF WASHINGTON
|
WA
|
$84,886
|
Muscular Dystrophy
|
NINDS
|
5P50NS040828-07
|
0001
|
Analysis and Therapy of Muscular Dystrophy in Zebrafish
|
KUNKEL, LOUIS
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$267,767
|
Muscular Dystrophy
|
NINDS
|
5P50NS040828-07
|
0002
|
Dysferlin: Approaches to Domain Analysis and Gene Therapy
|
BROWN, ROBERT
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$330,463
|
Muscular Dystrophy
|
NINDS
|
5P50NS040828-07
|
0004
|
Progenitor Cells inHuman Skeletal Muscle
|
GUSSONI, EMANUELA
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$276,233
|
Muscular Dystrophy
|
NINDS
|
5P50NS040828-07
|
9001
|
Clinical Specimen, Data Collection, and Expression Array Core
|
HOLM, INGRID
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$176,292
|
Muscular Dystrophy
|
NINDS
|
5P50NS040828-07
|
9002
|
Bioinformatics and Integrative/Comparative Genomics
|
KOHANE, ISAAC
|
CHILDREN'S HOSPITAL BOSTON
|
MA
|
$145,377
|
Muscular Dystrophy
|
NIAMS
|
1R21AR056055-01A1
|
|
Post-Translation Processing of Alpha-Dystroglycan
|
LIVE, DAVID
|
UNIVERSITY OF GEORGIA (UGA)
|
GA
|
$194,700
|
Muscular Dystrophy
|
NINDS
|
5U54NS053672-04
|
0001
|
Novel therapeutics strategies for Duchenne Muscular Dystrophy
|
CAMPBELL, KEVIN
|
UNIVERSITY OF IOWA
|
IA
|
$306,092
|
Muscular Dystrophy
|
NINDS
|
5U54NS053672-04
|
0002
|
Pathophysiology & therapeutics: Fukutin related protein(FKRP) muscular dystrophy
|
MATHEWS, KATHERINE
|
UNIVERSITY OF IOWA
|
IA
|
$303,401
|
Muscular Dystrophy
|
NINDS
|
5U54NS053672-04
|
0003
|
Therapeutic Potential of Embryonic Stem Cell-Derived Myogenic Precursors
|
YANG, BAOLI
|
UNIVERSITY OF IOWA
|
IA
|
$298,225
|
Muscular Dystrophy
|
NINDS
|
5U54NS053672-04
|
9001
|
Core--Muscle Biopsy/Cell Culture/ Diagnostics
|
MOORE, STEVEN
|
UNIVERSITY OF IOWA
|
IA
|
$241,321
|
Muscular Dystrophy
|
NINDS
|
5U54NS053672-04
|
9002
|
Core--Human ES Cell Targeting
|
WILLIAMSON, ROGER
|
UNIVERSITY OF IOWA
|
IA
|
$199,863
|
Muscular Dystrophy
|
NIAMS
|
1R01AR055299-01A1
|
|
Skeletal Muscle Regeneration from Differentiating Embryonic Stem Cells
|
PERLINGEIRO, RITA
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$332,200
|
Muscular Dystrophy
|
NIAMS
|
1R21AR057209-01A1
|
|
Exploring systemic AAV gene delivery in the dystrophic dog
|
DUAN, DONGSHENG
|
UNIVERSITY OF MISSOURI-COLUMBIA
|
MO
|
$175,887
|
Muscular Dystrophy
|
OD
|
3U54HD053177-03S1
|
|
Wellstone Muscular Dystrophy Center: Children's Nat'l Med Ctr
|
HOFFMAN, ERIC
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$6,000
|
Muscular Dystrophy
|
OD
|
2R56AR047664-06
|
|
Excitation-contraction Coupling in Normal and Dystrophic Mammalian Muscle
|
VERGARA, JULIO
|
UNIVERSITY OF CALIFORNIA LOS ANGELES
|
CA
|
$338,800
|
Muscular Dystrophy
|
NIAMS
|
3R01AR051368-04S1
|
|
Apoptosis in Laminin alpha2-Deficient Muscle Pathology
|
DOMINOV, JANICE
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$5,089
|
Muscular Dystrophy
|
NIAMS
|
5U54AR052646-04
|
0001
|
Targeting Myostatin Activation for Treatment of Muscular Dystraphy
|
LEE, SE-JIN
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$487,140
|
Muscular Dystrophy
|
NIAMS
|
5U54AR052646-04
|
0002
|
Protease Inhibition as Possible therapy for Muscular Dystrophy
|
SWEENEY, HUGH
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$470,464
|
Muscular Dystrophy
|
NIAMS
|
5U54AR052646-04
|
0003
|
Synergistic Effects of IGF-1 and Myostatin Modilation in Muscle
|
WAGNER, KATHRYN
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$353,366
|
Muscular Dystrophy
|
NIAMS
|
5U54AR052646-04
|
0004
|
Clinical Studies of Protease Inhibition in Duchenne Muscular Dystrophy
|
FISCHBECK, KENNETH
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$61,905
|
Muscular Dystrophy
|
NIAMS
|
5U54AR052646-04
|
9001
|
Physiological Assessment
|
BARTON, ELISABETH
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$186,049
|
Muscular Dystrophy
|
NIAMS
|
N01AR52274-6-0-1
|
|
National Registry for Myotonic Dystrophy & Facioscapulohumeral Muscular Dystrophy
|
NO PI IDENTIFIED
|
UNIVERSITY OF ROCHESTER
|
NY
|
$349,803
|
Muscular Dystrophy
|
NINDS
|
N01AR52274-6-0-1
|
|
National Registry for Myotonic Dystrophy & Facioscapulohumeral Muscular Dystrophy
|
NO PI IDENTIFIED
|
UNIVERSITY OF ROCHESTER
|
NY
|
$200,000
|
Muscular Dystrophy
|
NINDS
|
3R01NS033145-14S1
|
|
Regulation of Syntrophin Function
|
FROEHNER, STANLEY
|
UNIVERSITY OF WASHINGTON
|
WA
|
$38,864
|
Muscular Dystrophy
|
NIAMS
|
5U54NS058572-02
|
0001
|
Development of Novel Small Molecules for Delaying the Progression of Muscular Dys
|
SWEENEY, HUGH
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$51,019
|
Muscular Dystrophy
|
NINDS
|
5U54NS058572-02
|
0001
|
Development of Novel Small Molecules for Delaying the Progression of Muscular Dys
|
SWEENEY, HUGH
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$455,499
|
Muscular Dystrophy
|
NIAMS
|
5U54NS058572-02
|
9001
|
Biology Core
|
WELCH, ELLEN
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$48,877
|
Muscular Dystrophy
|
NINDS
|
5U54NS058572-02
|
9001
|
Biology Core
|
WELCH, ELLEN
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$436,378
|
Muscular Dystrophy
|
NIAMS
|
5U54NS058572-02
|
9002
|
Chemistry Core
|
YONG-CHOON, MOON
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$129,468
|
Muscular Dystrophy
|
NINDS
|
5U54NS058572-02
|
9002
|
Chemistry Core
|
YONG-CHOON, MOON
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$1,155,901
|
Muscular Dystrophy
|
NIAMS
|
5U54NS058572-02
|
9003
|
Pharmacology Core
|
WEETALL, MARLA
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$59,676
|
Muscular Dystrophy
|
NINDS
|
5U54NS058572-02
|
9003
|
Pharmacology Core
|
WEETALL, MARLA
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$532,789
|
Muscular Dystrophy
|
NIAMS
|
5U54AR050733-06
|
0001
|
Developing Clinical Outcomes for Gene Transfer
|
MENDELL, JERRY
|
UNIVERSITY OF PITTSBURGH AT PITTSBURGH
|
PA
|
$170,088
|
Muscular Dystrophy
|
NIAMS
|
5U54AR050733-06
|
0002
|
Preclinical Gene Therapy in a Large Animal Model of DMD
|
XIAO, XIAO
|
UNIVERSITY OF PITTSBURGH AT PITTSBURGH
|
PA
|
$4
|
Muscular Dystrophy
|
NIAMS
|
5U54AR050733-06
|
0003
|
Muscle Stem Cell-based therapies for Cardiomyopathy
|
HUARD, JOHNNY
|
UNIVERSITY OF PITTSBURGH AT PITTSBURGH
|
PA
|
$184,281
|
Muscular Dystrophy
|
NIAMS
|
5U54AR050733-06
|
9002
|
Cell and Tissue Imaging Core
|
WATKINS, SIMON
|
UNIVERSITY OF PITTSBURGH AT PITTSBURGH
|
PA
|
$62,097
|
Muscular Dystrophy
|
NIAMS
|
3R03AR053678-02S1
|
|
Expansion of Post-natal Human Stem Cells For A Pre-Clinical Dystrophy Model
|
DEASY, BRIDGET
|
CHILDREN'S HOSP PITTSBURGH/UPMC HLTH SYS
|
PA
|
$32,438
|
Muscular Dystrophy
|
NICHD
|
1U54HD060848-01
|
9002
|
Education and Training Core
|
BLOCH, ROBERT
|
BOSTON BIOMEDICAL RESEARCH INSTITUTE
|
MA
|
$172,390
|
Muscular Dystrophy
|
NINDS
|
5U54NS055958-02
|
0001
|
Dystrophin Restoration
|
MENDELL, JERRY
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$341,924
|
Muscular Dystrophy
|
NINDS
|
5U54NS055958-02
|
0002
|
CT GalNAc Transferase Gene Theraphy For DMD
|
MARTIN, PAUL
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$341,924
|
Muscular Dystrophy
|
NINDS
|
5U54NS055958-02
|
9002
|
Models Core
|
CHICOINE, LOUIS
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$341,927
|
Muscular Dystrophy
|
NINDS
|
5U54NS055958-02
|
9003
|
Immunology Core
|
WALKER, CHRISTOPHER
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$341,927
|
Muscular Dystrophy
|
NINDS
|
5U54NS055958-02
|
9004
|
Histopathology Core
|
SAHENK, ZARIFE
|
RESEARCH INST NATIONWIDE CHILDREN'S HOSP
|
OH
|
$341,928
|
Muscular Dystrophy
|
NINDS
|
1U01NS058451-01A1
|
0001
|
NF-kB Inhibition Therapy for Duchenne Muscular Dystrophy
|
GUTTRIDGE, DENIS
|
OHIO STATE UNIVERSITY
|
OH
|
$680,381
|
Muscular Dystrophy
|
NIAMS
|
1U24NS059696-01A1
|
0001
|
National Center for Canine Models of Duchenne Muscular Dystrophy (NCDMD)
|
KORNEGAY, JOE
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$300,000
|
Muscular Dystrophy
|
NINDS
|
1U24NS059696-01A1
|
0001
|
National Center for Canine Models of Duchenne Muscular Dystrophy (NCDMD)
|
KORNEGAY, JOE
|
UNIVERSITY OF NORTH CAROLINA CHAPEL HILL
|
NC
|
$691,633
|
Muscular Dystrophy
|
NICHD
|
5U54HD053177-04
|
0001
|
Genetic Modifiers
|
CHEN, JOSEPHINE%
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$448,749
|
Muscular Dystrophy
|
NICHD
|
5U54HD053177-04
|
0002
|
Cell Damage and Remodeling
|
CHEN, YI-WEN%
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$223,375
|
Muscular Dystrophy
|
NICHD
|
5U54HD053177-04
|
0003
|
Satellite Cell Biology
|
PARTRIDGE, TERENCE%
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$448,751
|
Muscular Dystrophy
|
NICHD
|
5U54HD053177-04
|
9001
|
Human Clinical Core
|
ESCOLAR, DIANA%
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$223,375
|
Muscular Dystrophy
|
NICHD
|
5U54HD053177-04
|
9002
|
Bio-informatics
|
CHEN, JOSEPHINE%
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$448,749
|
Muscular Dystrophy
|
NCRR
|
5M01RR020359-04
|
7267
|
CANDIDATE GENE AND PROTEIN STUDIES IN DISEASE
|
HOFFMAN, ERIC
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$2,738
|
Muscular Dystrophy
|
NCRR
|
5M01RR020359-04
|
7274
|
CNMC0601: A RANDOMIZED STUDY OF DAILY VS HIGH-DOSE WEEKLY PREDNISONE IN DUCHEN
|
ESCOLAR, DIANA
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$21,220
|
Muscular Dystrophy
|
NCRR
|
5M01RR020359-04
|
7295
|
3147K2-101-WW: A DOUBLE-BLIND, PLACEBO-CONTROLLED, RANDOMIZED, MULTIPLE ASCENDY
|
ESCOLAR, DIANA
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$21,220
|
Muscular Dystrophy
|
NCRR
|
5M01RR020359-04
|
7301
|
CNMC0705: A DOUBLE-BLINDED RANDOMIZED PLACEBO CONTROLLED STUDY OF DAILY
|
ESCOLAR, DIANA
|
CHILDREN'S RESEARCH INSTITUTE
|
DC
|
$58,186
|
Muscular Dystrophy
|
NCRR
|
5M01RR000400-40
|
7492
|
CNS DEGENERATION IN MYOTONIC DYSTROPHY TYPES 1 AND 2
|
DAY, JOHN
|
UNIVERSITY OF MINNESOTA TWIN CITIES
|
MN
|
$4,859
|
Muscular Dystrophy
|
NCRR
|
5M01RR000188-44
|
7777
|
CLINICAL TRIAL: DAILY VS WEEKLY PREDNISONE THERAPY IN DUCHENNE MUSCULAR DYSTROPH
|
LOTZE, TIMOTHY
|
BAYLOR COLLEGE OF MEDICINE
|
TX
|
$892
|
Muscular Dystrophy
|
NCRR
|
5M01RR023940-02
|
8463
|
CLINICAL TRIAL: GENTAMICIN IN DUCHENNE MD
|
BAROHN, RICHARD
|
UNIVERSITY OF KANSAS MEDICAL CENTER
|
KS
|
$24,932
|
Muscular Dystrophy
|
NCRR
|
5M01RR000064-44
|
8610
|
STUDY OF INHERITED NEUROLOGICAL DISEASES
|
FLANIGAN, KEVIN
|
UNIVERSITY OF UTAH
|
UT
|
$1,289
|
Muscular Dystrophy
|
NCRR
|
5M01RR000064-44
|
8618
|
CLINICAL TRIAL: BECKER FACIOSCAPULOHUMERAL AND LIMB-GIRDLE MUSCULAR DYSTROPHY
|
FLANIGAN, KEVIN
|
UNIVERSITY OF UTAH
|
UT
|
$6,017
|
Muscular Dystrophy
|
NCRR
|
5M01RR000064-44
|
8627
|
CLINICAL TRIAL: NONSENSE-MUTATION-MEDIATED DUCHENNE MUSCULAR DYSTROPHY
|
FLANIGAN, KEVIN
|
UNIVERSITY OF UTAH
|
UT
|
$23,124
|
Muscular Dystrophy
|
NCRR
|
5M01RR000034-48
|
8738
|
CLINICAL TRIAL: SIX-MONTH (26 WEEKS) CLINICAL TRIAL OF GENTAMICIN IN DUCHENNE MD
|
MENDELL, JERRY
|
OHIO STATE UNIVERSITY
|
OH
|
$1,733
|
Muscular Dystrophy
|
NCRR
|
5P20RR015567-09
|
6486
|
LOSARTAN IMPROVES VENTILATION IN DYSTROPHIC HAMSTERS
|
SCHLENKER, EVELYN
|
UNIVERSITY OF SOUTH DAKOTA
|
SD
|
$13,099
|
Muscular Dystrophy
|
NCRR
|
5P41RR006009-18
|
5443
|
STUDY OF TRINUCLEOTIDE REPEAT SEQUENCES USING THE GENERALIZED BORN MODEL
|
BOMBLE, YANNICK
|
CARNEGIE-MELLON UNIVERSITY
|
PA
|
$473
|
Muscular Dystrophy
|
NCRR
|
5P41RR002305-24
|
6010
|
MICROIMAGING & SPECTROSCOPY OF MUSCLE DAMAGE
|
WALTER, GLENN
|
UNIVERSITY OF PENNSYLVANIA
|
PA
|
$5,439
|
Muscular Dystrophy
|
NCRR
|
5P41RR013642-11
|
6582
|
MAPPING CALLOSAL THICKNESS IN PATIENTS WITH MYOTONIC DYSTROPHY TYPE 2
|
KORNBLUM, CORNELIA
|
UNIVERSITY OF CALIFORNIA LOS ANGELES
|
CA
|
$2,576
|
Muscular Dystrophy
|
NCRR
|
2P41RR012408-12
|
7826
|
PRP8, A CRITICAL PRE-MRNA SPLICING FACTOR
|
ZHAO, RUI
|
BROOKHAVEN SCIENCE ASSOC-BROOKHAVEN LAB
|
NY
|
$6,110
|
Muscular Dystrophy
|
NIAAA
|
1Z01AA000110-11
|
|
Metabolic Control Analysis
|
VEECH, RICHARD
|
NIH
|
|
$546,187
|
Muscular Dystrophy
|
NIAAA
|
1Z01AA000452-06
|
|
FRET imaging of protein-protein interactions inside living cells
|
VOGEL, STEVEN
|
NIH
|
|
$1,271,527
|
Muscular Dystrophy
|
NIAMS
|
1Z01AR027014-17
|
|
Molecular Mechanisms Of Myofibril Assembly And Function
|
HOROWITS, ROBERT
|
NIH
|
|
$863,879
|
Muscular Dystrophy
|
NHLBI
|
1Z01HL005906-01
|
|
Electron Microscopy Core
|
LO, CECILIA
|
NIH
|
|
$313,247
|